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    Tagged: gene therapy

    • The voices of AHC

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      • November 12, 2019
    • There was no cure for their daughters rare condition

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      • September 15, 2019
    • How CRISPR-Cas9 works

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      • May 11, 2019
    • Can we cure genetic diseases by rewriting DNA?

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      • May 11, 2019
    • AAV gene therapy for AHC – Any donation is a step forward

      • Associations / Interviews / News
      • November 4, 2018
    • Simon Frost at the ATP1A3 Symposium in Disease – Chicago 2018

      • Interviews
      • November 4, 2018
    • Dr Steven Gray talks about AAV gene therapy that can potentially help AHC patients.

      • Interviews
      • November 4, 2018

    Recent Posts

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    • Prof. Sanjay Sisodiya explains AHC
    • Dr. Al George – AHC interview 2019 – Reykjavik, Iceland
    • Dr. Steven Gray – ATP1A3 symposium in Reykjavik, Iceland
    • Sho Yano – ATP1A3 symposium in Reykjavik, Iceland

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